Treatment for Rare Diseases
As 80% of rare diseases are caused by a single gene and gene therapy has the capacity to heal cardinal genetic flaws, it makes sense to employ it to treat rare genetic disorders. Gene therapy can restore a single gene defect by introducing a "right" gene. A single dose may also be necessary for successful gene therapy to provide improvements that last a lifetime. Another method for treating uncommon disorders that uses RNA-based drug delivery is antisense therapies. The alternative method for treating rare disorders is called cell therapy, in which the patient receives an injection of live cells that have therapeutic effects.
- Rexin G
- Carmustine
- Nanotechnology and Nano-medicine
Related Conference of Treatment for Rare Diseases
September 10-11, 2024
5th Annual Meeting on Infectious Diseases, Microbiology & Beneficial Microbes
Amsterdam, Netherlands
October 17-18, 2024
12th World Congress on Control and Prevention of HIV/AIDS, STDs & STIs
London, UK
January 30-31, 2025
9th International Conference on Infectious Diseases: Control and Prevention
London, UK
May 21-22, 2025
12th International Conference on Infectious Diseases, Bacteriology and Antibiotics
Paris, France
Treatment for Rare Diseases Conference Speakers
Recommended Sessions
- Challenges in Rare Diseases
- Clinical Research on Rare Diseases
- Future of Rare Diseases Research
- Immune System Diseases
- Infectious Disease
- Living with Rare Diseases
- Mystery Diagnosis of Rare Diseases
- Orphan Drugs
- Rare Autoimmune Diseases
- Rare Cancer Diseases
- Rare Dermatological Diseases
- Rare Diseases
- Rare Diseases in Aging
- Rare Diseases in Brain
- Rare Diseases in Endocrine System
- Rare Gastrointestinal Diseases
- Rare Genetic Diseases
- Rare Haematological Diseases
- Rare Pediatric Diseases
- Treatment for Rare Diseases
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